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Novartis Position on Medicines for Patients with Rare Diseases

Novartis Public Affairs
Public Affairs Policy

Novartis Position on Medicines for Patients with
Rare Diseases
At Novartis our mission is to reimagine medicine to improve and extend patients’
lives. Using science-based innovation, we strive to deliver better outcomes for patients
and address the evolving healthcare needs of society.

Rare diseases are defined as life-threatening or chronically debilitating conditions that
affect only a small number of patients1. While individually...
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